Forschung & Innovation
Publikationen
A non-viral and selection-free COL7A1 HDR approach with improved safety profile for dystrophic epidermolysis bullosa.
PMU Autor*innen
Thomas Kocher, Johannes Bischof, Oliver March, Bernadette Liemberger, Stefan Hainzl, Julia Illmer, Anna Hoog, Katharina Muigg, Alfred Klausegger, Dirk Strunk, Johann Bauer, Ulrich Koller
Alle Autor*innen
Thomas Kocher, Johannes Bischof, Simone Alexandra Haas, Oliver March, Bernadette Liemberger, Stefan Hainzl, Julia Illmer, Anna Hoog, Katharina Muigg, Heide-Marie Binder, Alfred Klausegger, Dirk Strunk, Johann Bauer, Toni Cathomen, Ulrich Koller
Fachzeitschrift
Molecular Therapy - Nucleic Acids
Kurzfassung
Keywords
TRANSPLANTATION, STEM-CELLS, KERATINOCYTES, DNA, MUTATION, COL7A1, RETROVIRAL VECTORS, GENE CORRECTION, CRISPR CAS9, CAS9 NUCLEASE