Research & Innovation
Publications

A non-viral and selection-free COL7A1 HDR approach with improved safety profile for dystrophic epidermolysis bullosa.

#2021

#Molecular Therapy - Nucleic Acids

PMU Authors
Thomas Kocher, Johannes Bischof, Oliver March, Bernadette Liemberger, Stefan Hainzl, Julia Illmer, Anna Hoog, Katharina Muigg, Alfred Klausegger, Dirk Strunk, Johann Bauer, Ulrich Koller

All Authors
Thomas Kocher, Johannes Bischof, Simone Alexandra Haas, Oliver March, Bernadette Liemberger, Stefan Hainzl, Julia Illmer, Anna Hoog, Katharina Muigg, Heide-Marie Binder, Alfred Klausegger, Dirk Strunk, Johann Bauer, Toni Cathomen, Ulrich Koller

Journal association
Molecular Therapy - Nucleic Acids

Abstract

Keywords

TRANSPLANTATION, STEM-CELLS, KERATINOCYTES, DNA, MUTATION, COL7A1, RETROVIRAL VECTORS, GENE CORRECTION, CRISPR CAS9, CAS9 NUCLEASE

Latest Publication

#2025

#Abstract

Valentin Fischill-Neudeck, Antje van der Zee-Neuen, Margitta B. Beil-Hildebrand Strengthening Professional Health Literacy: A Theory-Based Approach to Empower Nursing Practice

#2025

#Original Article

Margaux Delporte, Johan Verbeeck, Isabella Brambilla, Georg Zimmermann, Geert Molenberghs, Rima Nabbout, Dravet syndrome, REGISTRY; RARE DISEASES; DRAVET SYNDROME; Natural history;

#2025

#Editorial

Eunkyeong Oh, Alberto Lucchini, Peter Nydahl Personalized approaches to ICU Distress

Back to Overview

Paracelsus Medical University (PMU) Research & Innovation Publications

A non-viral and selection-free COL7A1 HDR approach...