Paracelsus Medizinische Privatuniversität (PMU)

Forschung & Innovation
Publikationen

Cut and Paste: Efficient Homology-Directed Repair of a Dominant Negative KRT14 Mutation via CRISPR/Cas9 Nickases.

#2017
#MOLECULAR THERAPY

PMU Autor*innen
Thomas Kocher, Patricia Peking, Alfred Klausegger, Eva Maria Murauer, Josefina Piñón Hofbauer, Verena Wally, Thomas Lettner, Stefan Hainzl, Michael Ablinger, Johann Bauer, Julia Reichelt, Ulrich Koller

Alle Autor*innen
Thomas Kocher, Patricia Peking, Alfred Klausegger, Eva Maria Murauer, Josefina Piñón Hofbauer, Verena Wally, Thomas Lettner, Stefan Hainzl, Michael Ablinger, Johann Bauer, Julia Reichelt, Ulrich Koller

Fachzeitschrift
MOLECULAR THERAPY

Kurzfassung

Keywords

TRANSPLANTATION, FAMILY, KERATINOCYTES, SAFETY, DISORDERS, EPIDERMAL STEM-CELLS, GENE-THERAPY, EPIDERMOLYSIS-BULLOSA SIMPLEX, ENDONUCLEASE, KERATIN-14