Paracelsus Medizinische Privatuniversität (PMU)

Research & Innovation
Publications

Cut and Paste: Efficient Homology-Directed Repair of a Dominant Negative KRT14 Mutation via CRISPR/Cas9 Nickases.

#2017
#MOLECULAR THERAPY

PMU Authors
Thomas Kocher, Patricia Peking, Alfred Klausegger, Eva Maria Murauer, Josefina Piñón Hofbauer, Verena Wally, Thomas Lettner, Stefan Hainzl, Michael Ablinger, Johann Bauer, Julia Reichelt, Ulrich Koller

All Authors
Thomas Kocher, Patricia Peking, Alfred Klausegger, Eva Maria Murauer, Josefina Piñón Hofbauer, Verena Wally, Thomas Lettner, Stefan Hainzl, Michael Ablinger, Johann Bauer, Julia Reichelt, Ulrich Koller

Journal association
MOLECULAR THERAPY

Abstract

Keywords

TRANSPLANTATION, FAMILY, KERATINOCYTES, SAFETY, DISORDERS, EPIDERMAL STEM-CELLS, GENE-THERAPY, EPIDERMOLYSIS-BULLOSA SIMPLEX, ENDONUCLEASE, KERATIN-14