Research & Innovation
Publications

An RNA-targeted therapy for dystrophic epidermolysis bullosa.

#2017

#NUCLEIC ACIDS RESEARCH

PMU Authors
Patricia Peking, Ulrich Koller, Thomas Kocher, Gabriele Brachtl, Julia Reichelt, Johann Bauer, Eva Maria Murauer

All Authors
Patricia Peking, Ulrich Koller, Blanca Duarte, Rodolfo Murillas, Susanne Wolf, Tobias Maetzig, Michael Rothe, Thomas Kocher, Marta García, Gabriele Brachtl, Axel Schambach, Fernando Larcher, Julia Reichelt, Johann Bauer, Eva Maria Murauer

Journal association
NUCLEIC ACIDS RESEARCH

Abstract

Keywords

IN-VIVO ASSESSMENT, MOUSE MODEL, SAFETY, EPIDERMAL STEM-CELLS, GENE-THERAPY, HUMAN SKIN, COL7A1, VII COLLAGEN, LENTIVIRAL VECTORS, NC1 DOMAIN

Latest Publication

#2025

#Abstract

Valentin Fischill-Neudeck, Antje van der Zee-Neuen, Margitta B. Beil-Hildebrand Strengthening Professional Health Literacy: A Theory-Based Approach to Empower Nursing Practice

#2025

#Original Article

Margaux Delporte, Johan Verbeeck, Isabella Brambilla, Georg Zimmermann, Geert Molenberghs, Rima Nabbout, Dravet syndrome, REGISTRY; RARE DISEASES; DRAVET SYNDROME; Natural history;

#2025

#Editorial

Eunkyeong Oh, Alberto Lucchini, Peter Nydahl Personalized approaches to ICU Distress

Back to Overview

Paracelsus Medical University (PMU) Research & Innovation Publications

An RNA-targeted therapy for dystrophic...