Research & Innovation
Publications
An RNA-targeted therapy for dystrophic epidermolysis bullosa.
PMU Authors
Patricia Peking, Ulrich Koller, Thomas Kocher, Gabriele Brachtl, Julia Reichelt, Johann Bauer, Eva Maria Murauer
All Authors
Patricia Peking, Ulrich Koller, Blanca Duarte, Rodolfo Murillas, Susanne Wolf, Tobias Maetzig, Michael Rothe, Thomas Kocher, Marta García, Gabriele Brachtl, Axel Schambach, Fernando Larcher, Julia Reichelt, Johann Bauer, Eva Maria Murauer
Journal association
NUCLEIC ACIDS RESEARCH
Abstract
Keywords
IN-VIVO ASSESSMENT, MOUSE MODEL, SAFETY, EPIDERMAL STEM-CELLS, GENE-THERAPY, HUMAN SKIN, COL7A1, VII COLLAGEN, LENTIVIRAL VECTORS, NC1 DOMAIN