Paracelsus Medizinische Privatuniversität (PMU)

Research & Innovation
Publications

An RNA-targeted therapy for dystrophic epidermolysis bullosa.

#2017
#NUCLEIC ACIDS RESEARCH

PMU Authors
Patricia Peking, Ulrich Koller, Thomas Kocher, Gabriele Brachtl, Julia Reichelt, Johann Bauer, Eva Maria Murauer

All Authors
Patricia Peking, Ulrich Koller, Blanca Duarte, Rodolfo Murillas, Susanne Wolf, Tobias Maetzig, Michael Rothe, Thomas Kocher, Marta García, Gabriele Brachtl, Axel Schambach, Fernando Larcher, Julia Reichelt, Johann Bauer, Eva Maria Murauer

Journal association
NUCLEIC ACIDS RESEARCH

Abstract

Keywords

IN-VIVO ASSESSMENT, MOUSE MODEL, SAFETY, EPIDERMAL STEM-CELLS, GENE-THERAPY, HUMAN SKIN, COL7A1, VII COLLAGEN, LENTIVIRAL VECTORS, NC1 DOMAIN