Paracelsus Medizinische Privatuniversität (PMU)

Research & Innovation
Publications

Paired nicking-mediated COL17A1 reframing for junctional epidermolysis bullosa.

#2022
#MOLECULAR THERAPY

PMU Authors
Johannes Bischof, Oliver March, Bernadette Liemberger, Stefan Hainzl, Victoria Leb-Reichl, Julia Illmer, Evgeniia Korotchenko, Alfred Klausegger, Anna Hoog, Heide-Marie Binder, Dirk Strunk, Julia Reichelt, Christina Guttmann-Gruber, Verena Wally, Josefina Piñón Hofbauer, Johann Bauer, Thomas Kocher, Ulrich Koller

All Authors
Johannes Bischof, Oliver March, Bernadette Liemberger, Simone Alexandra Haas, Stefan Hainzl, Igor Petković, Victoria Leb-Reichl, Julia Illmer, Evgeniia Korotchenko, Alfred Klausegger, Anna Hoog, Heide-Marie Binder, Marta Garcia, Blanca Duarte, Dirk Strunk, Fernando Larcher, Julia Reichelt, Christina Guttmann-Gruber, Verena Wally, Josefina Piñón Hofbauer, Johann Bauer, Toni Cathomen, Thomas Kocher, Ulrich Koller

Journal association
MOLECULAR THERAPY

Abstract

Keywords

REPAIR, COLLAGEN XVII, CAS9