Research & Innovation
Publications
Paired nicking-mediated COL17A1 reframing for junctional epidermolysis bullosa.
PMU Authors
Johannes Bischof, Oliver March, Bernadette Liemberger, Stefan Hainzl, Victoria Leb-Reichl, Julia Illmer, Evgeniia Korotchenko, Alfred Klausegger, Anna Hoog, Heide-Marie Binder, Dirk Strunk, Julia Reichelt, Christina Guttmann-Gruber, Verena Wally, Josefina Piñón Hofbauer, Johann Bauer, Thomas Kocher, Ulrich Koller
All Authors
Johannes Bischof, Oliver March, Bernadette Liemberger, Simone Alexandra Haas, Stefan Hainzl, Igor Petković, Victoria Leb-Reichl, Julia Illmer, Evgeniia Korotchenko, Alfred Klausegger, Anna Hoog, Heide-Marie Binder, Marta Garcia, Blanca Duarte, Dirk Strunk, Fernando Larcher, Julia Reichelt, Christina Guttmann-Gruber, Verena Wally, Josefina Piñón Hofbauer, Johann Bauer, Toni Cathomen, Thomas Kocher, Ulrich Koller
Journal association
MOLECULAR THERAPY
Abstract
Keywords
REPAIR, COLLAGEN XVII, CAS9