Research & Innovation
Publications
Construction and validation of an RNA trans-splicing molecule suitable to repair a large number of COL7A1 mutations.
PMU Authors
Birgit Tockner, Thomas Kocher, Stefan Hainzl, Julia Reichelt, Johann Bauer, Ulrich Koller, Eva Maria Murauer
All Authors
Birgit Tockner, Thomas Kocher, Stefan Hainzl, Julia Reichelt, Johann Bauer, Ulrich Koller, Eva Maria Murauer
Journal association
GENE THERAPY
Abstract
Keywords
MOUSE MODEL, MESSENGER-RNA, SYSTEM, DEFICIENCY, IMPROVEMENT, DELIVERY, GENE-THERAPY, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, CELL THERAPY, TRANSPOSON