Paracelsus Medizinische Privatuniversität (PMU)

Research & Innovation
Publications

Construction and validation of an RNA trans-splicing molecule suitable to repair a large number of COL7A1 mutations.

#2016
#GENE THERAPY

PMU Authors
Birgit Tockner, Thomas Kocher, Stefan Hainzl, Julia Reichelt, Johann Bauer, Ulrich Koller, Eva Maria Murauer

All Authors
Birgit Tockner, Thomas Kocher, Stefan Hainzl, Julia Reichelt, Johann Bauer, Ulrich Koller, Eva Maria Murauer

Journal association
GENE THERAPY

Abstract

Keywords

MOUSE MODEL, MESSENGER-RNA, SYSTEM, DEFICIENCY, IMPROVEMENT, DELIVERY, GENE-THERAPY, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, CELL THERAPY, TRANSPOSON