Paracelsus Medizinische Privatuniversität (PMU)

Forschung & Innovation
Publikationen

Construction and validation of an RNA trans-splicing molecule suitable to repair a large number of COL7A1 mutations.

#2016
#GENE THERAPY

PMU Autor*innen
Birgit Tockner, Thomas Kocher, Stefan Hainzl, Julia Reichelt, Johann Bauer, Ulrich Koller, Eva Maria Murauer

Alle Autor*innen
Birgit Tockner, Thomas Kocher, Stefan Hainzl, Julia Reichelt, Johann Bauer, Ulrich Koller, Eva Maria Murauer

Fachzeitschrift
GENE THERAPY

Kurzfassung

Keywords

MOUSE MODEL, MESSENGER-RNA, SYSTEM, DEFICIENCY, IMPROVEMENT, DELIVERY, GENE-THERAPY, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, CELL THERAPY, TRANSPOSON