Forschung & Innovation
                                        
                                    
                                    
                                        
                                                Publikationen
                                            
                                    
                                
                            
                            
                        Construction and validation of an RNA trans-splicing molecule suitable to repair a large number of COL7A1 mutations.
                                        
                                        PMU Autor*innen
                                    
Birgit Tockner, Thomas Kocher, Stefan Hainzl, Julia Reichelt, Johann Bauer, Ulrich Koller, Eva Maria Murauer
Alle Autor*innen
Birgit Tockner, Thomas Kocher, Stefan Hainzl, Julia Reichelt, Johann Bauer, Ulrich Koller, Eva Maria Murauer
                                        Fachzeitschrift
                                    
GENE THERAPY                                                                                                                                                                                                                                              
Kurzfassung
Keywords
MOUSE MODEL, MESSENGER-RNA, SYSTEM, DEFICIENCY, IMPROVEMENT, DELIVERY, GENE-THERAPY, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, CELL THERAPY, TRANSPOSON