Forschung & Innovation
Publikationen
Gene editing for skin diseases: designer nucleases as tools for gene therapy of skin fragility disorders.
PMU Autor*innen
Julia Reichelt, Ulrich Koller
Alle Autor*innen
Oliver P March, Julia Reichelt, Ulrich Koller
Fachzeitschrift
EXPERIMENTAL PHYSIOLOGY
Kurzfassung
Keywords
TRANSPLANTATION, EPIDERMAL STEM-CELLS, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, RNA, EFFECTOR NUCLEASES, SPECIFICITY, KNOCKOUT