Paracelsus Medizinische Privatuniversität (PMU)

Forschung & Innovation
Publikationen

Gene editing for skin diseases: designer nucleases as tools for gene therapy of skin fragility disorders.

#2018
#EXPERIMENTAL PHYSIOLOGY

PMU Autor*innen
Julia Reichelt, Ulrich Koller

Alle Autor*innen
Oliver P March, Julia Reichelt, Ulrich Koller

Fachzeitschrift
EXPERIMENTAL PHYSIOLOGY

Kurzfassung

Keywords

TRANSPLANTATION, EPIDERMAL STEM-CELLS, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, RNA, EFFECTOR NUCLEASES, SPECIFICITY, KNOCKOUT