Forschung & Innovation
Publikationen
5'RNA Trans-Splicing Repair of COL7A1 Mutant Transcripts in Epidermolysis Bullosa
PMU Autor*innen
Elisabeth Mayr, Michael Ablinger, Thomas Lettner, Eva Maria Murauer, Christina Guttmann-Gruber, Josefina Piñón Hofbauer, Stefan Hainzl, Alfred Klausegger, Johann Bauer, Ulrich Koller, Verena Wally
Alle Autor*innen
Elisabeth Mayr, Michael Ablinger, Thomas Lettner, Eva Maria Murauer, Christina Guttmann-Gruber, Josefina Piñón Hofbauer, Stefan Hainzl, Manfred Kaiser, Alfred Klausegger, Johann Bauer, Ulrich Koller, Verena Wally
Fachzeitschrift
INTERNATIONAL JOURNAL OF MOLECULAR SCIENCES
Kurzfassung
Keywords
PROTEIN, Skin, DESIGN, MOUSE MODEL, MICE, CONSTRUCTION, GENE-THERAPY, VII COLLAGEN, RETROVIRAL VECTORS, MOLECULES