Forschung & Innovation
Publikationen
A Gene Gun-mediated Nonviral RNA trans-splicing Strategy for Col7a1 Repair.
PMU Autor*innen
Patricia Peking, Ulrich Koller, Stefan Hainzl, Thomas Kocher, Elisabeth Mayr, Thomas Lener, Julia Reichelt, Johann Bauer, Eva Maria Murauer
Alle Autor*innen
Patricia Peking, Ulrich Koller, Stefan Hainzl, Sophie Kitzmueller, Thomas Kocher, Elisabeth Mayr, Alexander Nyström, Thomas Lener, Julia Reichelt, Johann Bauer, Eva Maria Murauer
Fachzeitschrift
Molecular Therapy - Nucleic Acids
Kurzfassung
Keywords
IN-VIVO, THERAPY, REPLACEMENT, DISEASE, MOUSE MODEL, MESSENGER-RNA, DELIVERY, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, MUTATION DATABASE, MINICIRCLE DNA