Research & Innovation
Publications
A Gene Gun-mediated Nonviral RNA trans-splicing Strategy for Col7a1 Repair.
PMU Authors
Patricia Peking, Ulrich Koller, Stefan Hainzl, Thomas Kocher, Elisabeth Mayr, Thomas Lener, Julia Reichelt, Johann Bauer, Eva Maria Murauer
All Authors
Patricia Peking, Ulrich Koller, Stefan Hainzl, Sophie Kitzmueller, Thomas Kocher, Elisabeth Mayr, Alexander Nyström, Thomas Lener, Julia Reichelt, Johann Bauer, Eva Maria Murauer
Journal association
Molecular Therapy - Nucleic Acids
Abstract
Keywords
IN-VIVO, THERAPY, REPLACEMENT, DISEASE, MOUSE MODEL, MESSENGER-RNA, DELIVERY, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, MUTATION DATABASE, MINICIRCLE DNA