Forschung & Innovation
Publikationen
A novel screening system improves genetic correction by internal exon replacement.
PMU Autor*innen
Ulrich Koller, Verena Wally, Alfred Klausegger, Eva Maria Murauer, Elisabeth Mayr, Christina Gruber, Helmut Hintner, Johann Bauer
Alle Autor*innen
Ulrich Koller, Verena Wally, Lloyd G Mitchell, Alfred Klausegger, Eva Maria Murauer, Elisabeth Mayr, Christina Gruber, Stefan Hainzl, Helmut Hintner, Johann Bauer
Fachzeitschrift
NUCLEIC ACIDS RESEARCH
Kurzfassung
Keywords
THERAPY, REPAIR, EPIDERMOLYSIS-BULLOSA, PROSPECTS