Paracelsus Medizinische Privatuniversität (PMU)

Forschung & Innovation
Publikationen

Advances on potential therapeutic options for epidermolysis bullosa

#2018
#EXPERT OPINION ON ORPHAN DRUGS

PMU Autor*innen
Ulrich Koller, Johann Bauer, Julia Reichelt

Alle Autor*innen
L. De Rosa, Ulrich Koller, Johann Bauer, M. De Luca, Julia Reichelt

Fachzeitschrift
EXPERT OPINION ON ORPHAN DRUGS

Kurzfassung

Keywords

MOUSE MODEL, SPINAL MUSCULAR-ATROPHY, EPIDERMAL STEM-CELLS, RETROVIRAL VECTORS, CRISPR CAS9, VIVO GENE-THERAPY, REVERTANT MOSAICISM, SKIN FRAGILITY, PLEC1 GENE, RNA