Forschung & Innovation
Publikationen
Advances on potential therapeutic options for epidermolysis bullosa
PMU Autor*innen
Ulrich Koller, Johann Bauer, Julia Reichelt
Alle Autor*innen
L. De Rosa, Ulrich Koller, Johann Bauer, M. De Luca, Julia Reichelt
Fachzeitschrift
EXPERT OPINION ON ORPHAN DRUGS
Kurzfassung
Keywords
MOUSE MODEL, SPINAL MUSCULAR-ATROPHY, EPIDERMAL STEM-CELLS, RETROVIRAL VECTORS, CRISPR CAS9, VIVO GENE-THERAPY, REVERTANT MOSAICISM, SKIN FRAGILITY, PLEC1 GENE, RNA