Paracelsus Medizinische Privatuniversität (PMU)

Research & Innovation
Publications

Advances on potential therapeutic options for epidermolysis bullosa

#2018
#EXPERT OPINION ON ORPHAN DRUGS

PMU Authors
Ulrich Koller, Johann Bauer, Julia Reichelt

All Authors
L. De Rosa, Ulrich Koller, Johann Bauer, M. De Luca, Julia Reichelt

Journal association
EXPERT OPINION ON ORPHAN DRUGS

Abstract

Keywords

MOUSE MODEL, SPINAL MUSCULAR-ATROPHY, EPIDERMAL STEM-CELLS, RETROVIRAL VECTORS, CRISPR CAS9, VIVO GENE-THERAPY, REVERTANT MOSAICISM, SKIN FRAGILITY, PLEC1 GENE, RNA