Research & Innovation
Publications
Advances on potential therapeutic options for epidermolysis bullosa
PMU Authors
Ulrich Koller, Johann Bauer, Julia Reichelt
All Authors
L. De Rosa, Ulrich Koller, Johann Bauer, M. De Luca, Julia Reichelt
Journal association
EXPERT OPINION ON ORPHAN DRUGS
Abstract
Keywords
MOUSE MODEL, SPINAL MUSCULAR-ATROPHY, EPIDERMAL STEM-CELLS, RETROVIRAL VECTORS, CRISPR CAS9, VIVO GENE-THERAPY, REVERTANT MOSAICISM, SKIN FRAGILITY, PLEC1 GENE, RNA