Forschung & Innovation
Publikationen
An ex vivo RNA trans-splicing strategy to correct human generalized severe epidermolysis bullosa simplex.
PMU Autor*innen
Patricia Peking, Jenny Breitenbach, Michael Ablinger, Wolfgang Muss, Thomas Kocher, Ulrich Koller, Stefan Hainzl, Johann Bauer, Julia Reichelt, Thomas Lettner, Verena Wally
Alle Autor*innen
Patricia Peking, Jenny Breitenbach, Michael Ablinger, Wolfgang Muss, F J Poetschke, Thomas Kocher, Ulrich Koller, Stefan Hainzl, S. Kitzmueller, Johann Bauer, Julia Reichelt, Thomas Lettner, Verena Wally
Fachzeitschrift
BRITISH JOURNAL OF DERMATOLOGY
Kurzfassung
Keywords
CELLS, TRANSPLANTATION, REPAIR, MOUSE MODEL, KERATINOCYTES, DEFICIENCY, IMPROVEMENT, GENE-THERAPY, COL7A1, DIACEREIN