Research & Innovation
Publications
An ex vivo RNA trans-splicing strategy to correct human generalized severe epidermolysis bullosa simplex.
PMU Authors
Patricia Peking, Jenny Breitenbach, Michael Ablinger, Wolfgang Muss, Thomas Kocher, Ulrich Koller, Stefan Hainzl, Johann Bauer, Julia Reichelt, Thomas Lettner, Verena Wally
All Authors
Patricia Peking, Jenny Breitenbach, Michael Ablinger, Wolfgang Muss, F J Poetschke, Thomas Kocher, Ulrich Koller, Stefan Hainzl, S. Kitzmueller, Johann Bauer, Julia Reichelt, Thomas Lettner, Verena Wally
Journal association
BRITISH JOURNAL OF DERMATOLOGY
Abstract
Keywords
CELLS, TRANSPLANTATION, REPAIR, MOUSE MODEL, KERATINOCYTES, DEFICIENCY, IMPROVEMENT, GENE-THERAPY, COL7A1, DIACEREIN