Paracelsus Medizinische Privatuniversität (PMU)

Research & Innovation
Publications

An ex vivo RNA trans-splicing strategy to correct human generalized severe epidermolysis bullosa simplex.

#2019
#BRITISH JOURNAL OF DERMATOLOGY

PMU Authors
Patricia Peking, Jenny Breitenbach, Michael Ablinger, Wolfgang Muss, Thomas Kocher, Ulrich Koller, Stefan Hainzl, Johann Bauer, Julia Reichelt, Thomas Lettner, Verena Wally

All Authors
Patricia Peking, Jenny Breitenbach, Michael Ablinger, Wolfgang Muss, F J Poetschke, Thomas Kocher, Ulrich Koller, Stefan Hainzl, S. Kitzmueller, Johann Bauer, Julia Reichelt, Thomas Lettner, Verena Wally

Journal association
BRITISH JOURNAL OF DERMATOLOGY

Abstract

Keywords

CELLS, TRANSPLANTATION, REPAIR, MOUSE MODEL, KERATINOCYTES, DEFICIENCY, IMPROVEMENT, GENE-THERAPY, COL7A1, DIACEREIN