Paracelsus Medizinische Privatuniversität (PMU)

Forschung & Innovation
Publikationen

Gentamicin induces LAMB3 nonsense mutation readthrough and restores functional laminin 332 in junctional epidermolysis bullosa

#2018
#PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA

PMU Autor*in
Johann Bauer

Alle Autor*innen
V. Lincoln, J. Cogan, YP Hou, M. Hirsch, M. Hao, V. Alexeev, M. De Luca, L. De Rosa, Johann Bauer, DT Woodley, M. Chen

Fachzeitschrift
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA

Kurzfassung

Keywords

DOUBLE-BLIND, CYSTIC-FIBROSIS, EPIDERMAL STEM-CELLS, CLINICAL-COURSE, PREMATURE TERMINATION CODONS, VII COLLAGEN, MUSCULAR-DYSTROPHY, DECISION-MAKING, PHASE-3 TRIAL, READ-THROUGH