Forschung & Innovation
Publikationen
Improved Double-Nicking Strategies for COL7A1-Editing by Homologous Recombination.
PMU Autor*innen
Thomas Kocher, Alfred Klausegger, Christina Guttmann-Gruber, Stefan Hainzl, Johann Bauer, Julia Reichelt, Ulrich Koller
Alle Autor*innen
Thomas Kocher, Roland N Wagner, Alfred Klausegger, Christina Guttmann-Gruber, Stefan Hainzl, Johann Bauer, Julia Reichelt, Ulrich Koller
Fachzeitschrift
Molecular Therapy - Nucleic Acids
Kurzfassung
Keywords
STEM-CELLS, REPAIR, COLLAGEN, MUTATION, COL7A1, CAS9, CRISPR/CAS9, EPIDERMOLYSIS-BULLOSA, FIBROBLAST CELL THERAPY, WEB TOOL