Paracelsus Medizinische Privatuniversität (PMU)

Research & Innovation
Publications

Improved Double-Nicking Strategies for COL7A1-Editing by Homologous Recombination.

#2019
#Molecular Therapy - Nucleic Acids

PMU Authors
Thomas Kocher, Alfred Klausegger, Christina Guttmann-Gruber, Stefan Hainzl, Johann Bauer, Julia Reichelt, Ulrich Koller

All Authors
Thomas Kocher, Roland N Wagner, Alfred Klausegger, Christina Guttmann-Gruber, Stefan Hainzl, Johann Bauer, Julia Reichelt, Ulrich Koller

Journal association
Molecular Therapy - Nucleic Acids

Abstract

Keywords

STEM-CELLS, REPAIR, COLLAGEN, MUTATION, COL7A1, CAS9, CRISPR/CAS9, EPIDERMOLYSIS-BULLOSA, FIBROBLAST CELL THERAPY, WEB TOOL