Forschung & Innovation
Publikationen
RNA-based therapies for genodermatoses.
PMU Autor*innen
Patricia Peking, Ulrich Koller, Eva Maria Murauer
Alle Autor*innen
Olivier Bornert, Patricia Peking, Jeroen Bremer, Ulrich Koller, Peter C van den Akker, Annemieke Aartsma-Rus, Anna M G Pasmooij, Eva Maria Murauer, Alexander Nyström
Fachzeitschrift
EXPERIMENTAL DERMATOLOGY
Kurzfassung
Keywords
MOUSE MODEL, GENE-THERAPY, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, PREMATURE TERMINATION CODONS, VII COLLAGEN, DUCHENNE MUSCULAR-DYSTROPHY, DERMAL-EPIDERMAL JUNCTION, SKIN ADHESION DISORDERS, MODIFIED MESSENGER-RNA, ANTISENSE OLIGONUCLEOTIDES