Paracelsus Medizinische Privatuniversität (PMU)

Forschung & Innovation
Publikationen

RNA-based therapies for genodermatoses.

#2017
#EXPERIMENTAL DERMATOLOGY

PMU Autor*innen
Patricia Peking, Ulrich Koller, Eva Maria Murauer

Alle Autor*innen
Olivier Bornert, Patricia Peking, Jeroen Bremer, Ulrich Koller, Peter C van den Akker, Annemieke Aartsma-Rus, Anna M G Pasmooij, Eva Maria Murauer, Alexander Nyström

Fachzeitschrift
EXPERIMENTAL DERMATOLOGY

Kurzfassung

Keywords

MOUSE MODEL, GENE-THERAPY, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, PREMATURE TERMINATION CODONS, VII COLLAGEN, DUCHENNE MUSCULAR-DYSTROPHY, DERMAL-EPIDERMAL JUNCTION, SKIN ADHESION DISORDERS, MODIFIED MESSENGER-RNA, ANTISENSE OLIGONUCLEOTIDES