Forschung & Innovation
Publikationen
A reporter-based screen to identify potent 3" trans-splicing molecules for endogenous RNA repair.
PMU Autor*innen
Eva Maria Murauer, Ulrich Koller, Stefan Hainzl, Verena Wally, Johann Bauer
Alle Autor*innen
Eva Maria Murauer, Ulrich Koller, Stefan Hainzl, Verena Wally, Johann Bauer
Fachzeitschrift
HUMAN GENE THERAPY METHODS
Kurzfassung
Keywords
IN-VIVO, INJECTION, EXPRESSION, GENE-THERAPY, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, COL7A1, RETROVIRAL VECTORS, VII, RESTORATION