Paracelsus Medizinische Privatuniversität (PMU)

Forschung & Innovation
Publikationen

A reporter-based screen to identify potent 3" trans-splicing molecules for endogenous RNA repair.

#2013
#HUMAN GENE THERAPY METHODS

PMU Autor*innen
Eva Maria Murauer, Ulrich Koller, Stefan Hainzl, Verena Wally, Johann Bauer

Alle Autor*innen
Eva Maria Murauer, Ulrich Koller, Stefan Hainzl, Verena Wally, Johann Bauer

Fachzeitschrift
HUMAN GENE THERAPY METHODS

Kurzfassung

Keywords

IN-VIVO, INJECTION, EXPRESSION, GENE-THERAPY, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, COL7A1, RETROVIRAL VECTORS, VII, RESTORATION