Research & Innovation
Publications
A reporter-based screen to identify potent 3" trans-splicing molecules for endogenous RNA repair.
PMU Authors
Eva Maria Murauer, Ulrich Koller, Stefan Hainzl, Verena Wally, Johann Bauer
All Authors
Eva Maria Murauer, Ulrich Koller, Stefan Hainzl, Verena Wally, Johann Bauer
Journal association
HUMAN GENE THERAPY METHODS
Abstract
Keywords
IN-VIVO, INJECTION, EXPRESSION, GENE-THERAPY, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, COL7A1, RETROVIRAL VECTORS, VII, RESTORATION