Paracelsus Medizinische Privatuniversität (PMU)

Research & Innovation
Publications

A reporter-based screen to identify potent 3" trans-splicing molecules for endogenous RNA repair.

#2013
#HUMAN GENE THERAPY METHODS

PMU Authors
Eva Maria Murauer, Ulrich Koller, Stefan Hainzl, Verena Wally, Johann Bauer

All Authors
Eva Maria Murauer, Ulrich Koller, Stefan Hainzl, Verena Wally, Johann Bauer

Journal association
HUMAN GENE THERAPY METHODS

Abstract

Keywords

IN-VIVO, INJECTION, EXPRESSION, GENE-THERAPY, DYSTROPHIC EPIDERMOLYSIS-BULLOSA, COL7A1, RETROVIRAL VECTORS, VII, RESTORATION