Paracelsus Medizinische Privatuniversität (PMU)

Forschung & Innovation
Publikationen

Clinical Perspectives of Gene-Targeted Therapies for Epidermolysis Bullosa.

#2021
#DERMATOLOGY AND THERAPY

PMU Autor*innen
Tobias Welponer, Christine Prodinger, Josefina Pinon-Hofbauer, Arno Maria Hintersteininger, Johann Bauer, Martin Laimer

Alle Autor*innen
Tobias Welponer, Christine Prodinger, Josefina Pinon-Hofbauer, Arno Maria Hintersteininger, Hannelore Breitenbach-Koller, Johann Bauer, Martin Laimer

Fachzeitschrift
DERMATOLOGY AND THERAPY

Kurzfassung

Keywords

DISEASE, MOUSE MODEL, MUTATION, EPIDERMAL STEM-CELLS, COL7A1, VII COLLAGEN, REVERTANT MOSAICISM, EXTRACUTANEOUS MANIFESTATIONS, HOMOLOGY-DIRECTED REPAIR, FIBROBLAST CELL THERAPY