Paracelsus Medizinische Privatuniversität (PMU)

Research & Innovation
Publications

Clinical Perspectives of Gene-Targeted Therapies for Epidermolysis Bullosa.

#2021
#DERMATOLOGY AND THERAPY

PMU Authors
Tobias Welponer, Christine Prodinger, Josefina Pinon-Hofbauer, Arno Maria Hintersteininger, Johann Bauer, Martin Laimer

All Authors
Tobias Welponer, Christine Prodinger, Josefina Pinon-Hofbauer, Arno Maria Hintersteininger, Hannelore Breitenbach-Koller, Johann Bauer, Martin Laimer

Journal association
DERMATOLOGY AND THERAPY

Abstract

Keywords

DISEASE, MOUSE MODEL, MUTATION, EPIDERMAL STEM-CELLS, COL7A1, VII COLLAGEN, REVERTANT MOSAICISM, EXTRACUTANEOUS MANIFESTATIONS, HOMOLOGY-DIRECTED REPAIR, FIBROBLAST CELL THERAPY