Research & Innovation
Publications
Clinical Perspectives of Gene-Targeted Therapies for Epidermolysis Bullosa.
PMU Authors
Tobias Welponer, Christine Prodinger, Josefina Pinon-Hofbauer, Arno Maria Hintersteininger, Johann Bauer, Martin Laimer
All Authors
Tobias Welponer, Christine Prodinger, Josefina Pinon-Hofbauer, Arno Maria Hintersteininger, Hannelore Breitenbach-Koller, Johann Bauer, Martin Laimer
Journal association
DERMATOLOGY AND THERAPY
Abstract
Keywords
DISEASE, MOUSE MODEL, MUTATION, EPIDERMAL STEM-CELLS, COL7A1, VII COLLAGEN, REVERTANT MOSAICISM, EXTRACUTANEOUS MANIFESTATIONS, HOMOLOGY-DIRECTED REPAIR, FIBROBLAST CELL THERAPY