Research & Innovation
Publications
Highly efficient paired nickase-mediated correction of junctional epidermolysis bullosa via COL17A1 reframing
PMU Authors
Oliver March, Thomas Kocher, Bernadette Liemberger, Johannes Bischof, Stefan Hainzl, Anna Hochreiter, Dirk Strunk, Julia Reichelt, Johann Bauer, Ulrich Koller
All Authors
Oliver March, Thomas Kocher, Bernadette Liemberger, Johannes Bischof, Stefan Hainzl, S. Haas, Anna Hochreiter, Dirk Strunk, T. Cathomen, Julia Reichelt, Johann Bauer, Ulrich Koller
Journal association
HUMAN GENE THERAPY
Abstract
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