Paracelsus Medizinische Privatuniversität (PMU)

Research & Innovation
Publications

Highly efficient paired nickase-mediated correction of junctional epidermolysis bullosa via COL17A1 reframing

#2019
#HUMAN GENE THERAPY

PMU Authors
Oliver March, Thomas Kocher, Bernadette Liemberger, Johannes Bischof, Stefan Hainzl, Anna Hochreiter, Dirk Strunk, Julia Reichelt, Johann Bauer, Ulrich Koller

All Authors
Oliver March, Thomas Kocher, Bernadette Liemberger, Johannes Bischof, Stefan Hainzl, S. Haas, Anna Hochreiter, Dirk Strunk, T. Cathomen, Julia Reichelt, Johann Bauer, Ulrich Koller

Journal association
HUMAN GENE THERAPY

Abstract

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