Paracelsus Medizinische Privatuniversität (PMU)

Research & Innovation
Publications

Toward Combined Cell and Gene Therapy for Genodermatoses.

#2020
#COLD SPRING HARBOR PERSPECTIVES IN BIOLOGY

PMU Author
Johann Bauer

All Authors
Laura De Rosa, Maria Carmela Latella, Alessia Secone Seconetti, Cecilia Cattelani, Johann Bauer, Sergio Bondanza, Michele De Luca

Journal association
COLD SPRING HARBOR PERSPECTIVES IN BIOLOGY

Abstract

Keywords

PROGENITOR CELLS, EPIDERMAL STEM-CELLS, VII COLLAGEN, HOMOLOGY-DIRECTED REPAIR, INHERITED EPIDERMOLYSIS-BULLOSA, INACTIVATING RETROVIRAL VECTORS, ALPHARETROVIRAL VECTORS, ADENOSINE-DEAMINASE, HEMATOPOIETIC STEM, NEXT-GENERATION