Research & Innovation
Publications
Toward Combined Cell and Gene Therapy for Genodermatoses.
PMU Author
Johann Bauer
All Authors
Laura De Rosa, Maria Carmela Latella, Alessia Secone Seconetti, Cecilia Cattelani, Johann Bauer, Sergio Bondanza, Michele De Luca
Journal association
COLD SPRING HARBOR PERSPECTIVES IN BIOLOGY
Abstract
Keywords
PROGENITOR CELLS, EPIDERMAL STEM-CELLS, VII COLLAGEN, HOMOLOGY-DIRECTED REPAIR, INHERITED EPIDERMOLYSIS-BULLOSA, INACTIVATING RETROVIRAL VECTORS, ALPHARETROVIRAL VECTORS, ADENOSINE-DEAMINASE, HEMATOPOIETIC STEM, NEXT-GENERATION