Research & Innovation
Publications
Diacerein orphan drug development for epidermolysis bullosa simplex: A phase 2/3 randomized, placebo-controlled, double-blind clinical trial.
PMU Authors
Verena Wally, Thomas Lettner, Michael Ablinger, Thomas Felder, Florian Lagler, Wolfgang Hitzl, Martin Laimer, Sophie Kitzmüller, Anja Diem, Johann Bauer
All Authors
Verena Wally, Alain Hovnanian, Juliette Ly, Hana Buckova, Victoria Brunner, Thomas Lettner, Michael Ablinger, Thomas Felder, Peter Hofbauer, Martin Wolkersdorfer, Florian Lagler, Wolfgang Hitzl, Martin Laimer, Sophie Kitzmüller, Anja Diem, Johann Bauer
Journal association
JOURNAL OF THE AMERICAN ACADEMY OF DERMATOLOGY
Abstract
Keywords
GENE, MUTATIONS, SAFETY, AMPLIFICATION, DISORDERS, EPIDERMAL STEM-CELLS, DOWLING-MEARA, KERATIN-5, EBS