Paracelsus Medizinische Privatuniversität (PMU)

Research & Innovation
Publications

Diacerein orphan drug development for epidermolysis bullosa simplex: A phase 2/3 randomized, placebo-controlled, double-blind clinical trial.

#2018
#JOURNAL OF THE AMERICAN ACADEMY OF DERMATOLOGY

PMU Authors
Verena Wally, Thomas Lettner, Michael Ablinger, Thomas Felder, Florian Lagler, Wolfgang Hitzl, Martin Laimer, Sophie Kitzmüller, Anja Diem, Johann Bauer

All Authors
Verena Wally, Alain Hovnanian, Juliette Ly, Hana Buckova, Victoria Brunner, Thomas Lettner, Michael Ablinger, Thomas Felder, Peter Hofbauer, Martin Wolkersdorfer, Florian Lagler, Wolfgang Hitzl, Martin Laimer, Sophie Kitzmüller, Anja Diem, Johann Bauer

Journal association
JOURNAL OF THE AMERICAN ACADEMY OF DERMATOLOGY

Abstract

Keywords

GENE, MUTATIONS, SAFETY, AMPLIFICATION, DISORDERS, EPIDERMAL STEM-CELLS, DOWLING-MEARA, KERATIN-5, EBS