Paracelsus Medizinische Privatuniversität (PMU)

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Publications

Efficient correction of a prevalent COL7A1 mutation via prime editing in recessive dystrophic epidermolysis bullosa

#2025
#HUMAN GENE THERAPY

PMU Authors
J. Bischof, T. Kocher, L. Lopes Pedroso, B. Liemberger, S. Hainzl, M. Hierl, N. Maeding, D. Strunk, C. Guttmann-Gruber, V. Wally, J. Pinon Hofbauer, J. W. Bauer, U. Koller

All Authors
J. Bischof, T. Kocher, L. Lopes Pedroso, B. Liemberger, S. Hainzl, M. Hierl, N. Maeding, D. Strunk, C. Guttmann-Gruber, V. Wally, J. Pinon Hofbauer, J. W. Bauer, U. Koller

Journal association
HUMAN GENE THERAPY

Abstract

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